New Gene Therapy at a World-Renowned Research Insitute
07 August 2019
There is a new NF2 Gene Therapy Pilot Pre-Clinical Study at the Abigail Wexner Research Institute at Nationwide Children’s Hospital (NCH) by Dr. Kathrin Meyer, who is serving as the Principal Investigator.
This lab is considered to be one of the top gene therapy labs in the world, therefore NF2 patients and families can be assured that the best gene therapy researchers are working on curing NF2, but NF2 Biosolutions needs your support to help fund these projects.
Dr. Meyer will be the principal investigator for this NF2 project. Dr Meyer focuses on studying disease mechanisms in neurodegenerative diseases and finding new innovative therapeutic strategies for them. A main emphasis is understanding the impact of different mutations on disease course and severity. Moreover, Dr. Meyer’s lab has a strong translational focus in her projects with the goal to move additional programs towards clinical trials. These projects include the optimization of delivery strategies and evaluation of efficacy and targeting of various areas of the nervous system with gene therapy.
Dr. Kathrin Meyer

Investigators at the Center for Gene Therapy in The Research Institute at Nationwide Children’s Hospital are currently conducting numerous clinical research studies on other diseases like Batten, Charcot-Marie-Tooth Neuropathy Type 1, Duchenne Muscular Dystrophy, Mucopolysaccharidosis (MPS). See the list here.
The recently FDA approved gene therapy for treatment of the fatal genetic disorder SMA was developed at Nationwide Children’s Hospital. This approval was groundbreaking and is the first and only systemically administered gene therapy approved by the FDA in the US.
Read more about how NCH became ground zero for gene therapy by clicking on the link below:
This is also a therapy that NF2 Biosolutions are strongly endorsing, we would strongly encourage you to visit their website by clicking on the link below:
Filter News

NF1 PN Impact on Patients’ and Caregivers’ Lives
If you have NF1 with plexiform neurofibromas or you care for someone with NF1 PN help shape future healthcare support
Read More
24 Hour Marathon – Three Brothers Running for the Fourth
Toby, James & Alex take on an epic 24 hour marathon race to commemorate their brother Tristan
Read More
Centre for Appearance Research NF Survey - Results
Find out how you can take part in CAR's online survey about NF parenting and caring experiences.
Read More
Share your Covid-19 Story - Survey Results
Embracing Complexity share the results of their impact of Covid19 survey, find out more
Read More
Hour of Power – Love Yourself Valentine’s Day workout for NF
Thanks to all those that got their hearts pumping this Valentine's Day for our NF community!
Read More
Rare Disease Day 2021 and Rare Reach Festival
Find out how you can get involved in the first ever Rare Reach Festival and make sure the Rare communities voice is heard!
Read More
NF Said
Daisy takes on a 38-mile running challenge for her sister Millie, 1 mile a day for every person diagnosed with NF2 a year
Read More