New Gene Therapy at a World-Renowned Research Insitute
07 August 2019
There is a new NF2 Gene Therapy Pilot Pre-Clinical Study at the Abigail Wexner Research Institute at Nationwide Children’s Hospital (NCH) by Dr. Kathrin Meyer, who is serving as the Principal Investigator.
This lab is considered to be one of the top gene therapy labs in the world, therefore NF2 patients and families can be assured that the best gene therapy researchers are working on curing NF2, but NF2 Biosolutions needs your support to help fund these projects.
Dr. Meyer will be the principal investigator for this NF2 project. Dr Meyer focuses on studying disease mechanisms in neurodegenerative diseases and finding new innovative therapeutic strategies for them. A main emphasis is understanding the impact of different mutations on disease course and severity. Moreover, Dr. Meyer’s lab has a strong translational focus in her projects with the goal to move additional programs towards clinical trials. These projects include the optimization of delivery strategies and evaluation of efficacy and targeting of various areas of the nervous system with gene therapy.
Dr. Kathrin Meyer
Investigators at the Center for Gene Therapy in The Research Institute at Nationwide Children’s Hospital are currently conducting numerous clinical research studies on other diseases like Batten, Charcot-Marie-Tooth Neuropathy Type 1, Duchenne Muscular Dystrophy, Mucopolysaccharidosis (MPS). See the list here.
The recently FDA approved gene therapy for treatment of the fatal genetic disorder SMA was developed at Nationwide Children’s Hospital. This approval was groundbreaking and is the first and only systemically administered gene therapy approved by the FDA in the US.
Read more about how NCH became ground zero for gene therapy by clicking on the link below:
This is also a therapy that NF2 Biosolutions are strongly endorsing, we would strongly encourage you to visit their website by clicking on the link below:
Filter News
NF Said
Daisy takes on a 38-mile running challenge for her sister Millie, 1 mile a day for every person diagnosed with NF2 a year
Read MoreLove Yourself - Hour of Power in Support of the NF community
Get your sweat on and spread the love this Valentine's day for our NF community!
Read MorePat’s NF Fundraiser Walk
Read all about Patrick's incredible fundraising efforts to help others affected by NF!
Read MoreLaura’s Marathon effort!
Laura beats our 26.5 mile challenge and takes it to the next level - matching miles with donations, find out what she's up to
Read MoreResearch call: Does neurofibromatosis affect how you feel about your body?
Find out how you can improve self-help methods for people living with neurofibromatosis
Read MoreStitched up by Celia
Get inspired by Celia's creative online haberdashery shop for Nerve Tumours UK!
Read MoreNF1 with Plexiform Neurofibromas Study: information for patients and carers
Find out how you can help shape the future of NF1 healthcare
Read MoreChanging Faces Impact of Covid Survey
Share your experience of covid19 with Changing Faces and help shape the support you need
Read MoreBe as creative as Faye – Follow her social distance fundraising example!
Be inspired by Faye & take on your own creative fundraising idea this lockdown!
Read More