Helpline 07939 046 030

New Gene Therapy at a World-Renowned Research Insitute

07 August 2019

There is a new NF2 Gene Therapy Pilot Pre-Clinical Study at the Abigail Wexner Research Institute at Nationwide Children’s Hospital (NCH) by Dr. Kathrin Meyer, who is serving as the Principal Investigator.

This lab is considered to be one of the top gene therapy labs in the world, therefore NF2 patients and families can be assured that the best gene therapy researchers are working on curing NF2, but NF2 Biosolutions needs your support to help fund these projects.

Dr. Meyer will be the principal investigator for this NF2 project. Dr Meyer focuses on studying disease mechanisms in neurodegenerative diseases and finding new innovative therapeutic strategies for them. A main emphasis is understanding the impact of different mutations on disease course and severity. Moreover, Dr. Meyer’s lab has a strong translational focus in her projects with the goal to move additional programs towards clinical trials. These projects include the optimization of delivery strategies and evaluation of efficacy and targeting of various areas of the nervous system with gene therapy.

Dr. Kathrin Meyer

Investigators at the Center for Gene Therapy in The Research Institute at Nationwide Children’s Hospital are currently conducting numerous clinical research studies on other diseases like Batten, Charcot-Marie-Tooth Neuropathy Type 1, Duchenne Muscular Dystrophy, Mucopolysaccharidosis (MPS). See the list here.

The recently FDA approved gene therapy for treatment of the fatal genetic disorder SMA was developed at Nationwide Children’s Hospital. This approval was groundbreaking and is the first and only systemically administered gene therapy approved by the FDA in the US.

Read more about how NCH became ground zero for gene therapy by clicking on the link below:

This is also a therapy that NF2 Biosolutions are strongly endorsing, we would strongly encourage you to visit their website by clicking on the link below:

Filter News

Filter by Date
Category
Reset

Tim’s Story: Living With Neurofibromatosis – it’s a family thing

Tim tells us how Nerve Tumours UK proved to be an invaluable resource and support to him and his family as he was growing up

Read More

Dalvinder’s 100km Ultra Challenge for NF

Dalvinder on the 100km Ultra Challenge Thames Path walk to raise money for NF

Read More

Esme’s Summer of Slides

Esme's Summer of Sliding for NTUK!

Read More

Diana’s One Month of Rowing for Neurofibromatosis

Diana is taking on an epic 150k rowing challenge - 5k per day to support her daughter Ellie & our NF community

Read More

Kian’s NF2 Blog

Kian shares his NF2 journey and his inspirational path - training to swim in the para-olympics

Read More

Autistica Research Festival 2021

See how this year's event went and find out how you can watch the best bits if you couldn't make the conference.

Read More

OneMoreNurse joins the NTUK team in Leeds

We're delighted to announce our new Specialist NF Nurse for Leeds, find out more

Read More

The NTUK running team kick starts 2021’s running season in this year’s Asics 10k!

Check out the year's first major running event - see how our NTUK running team got on!

Read More

Alex’s 12 months of Running

Alex has nearly completed his incredible 12 months of running for NTUK, totalling a whopping 80km – see how he got on!

Read More