Helpline 07939 046 030

New Gene Therapy at a World-Renowned Research Insitute

07 August 2019

There is a new NF2 Gene Therapy Pilot Pre-Clinical Study at the Abigail Wexner Research Institute at Nationwide Children’s Hospital (NCH) by Dr. Kathrin Meyer, who is serving as the Principal Investigator.

This lab is considered to be one of the top gene therapy labs in the world, therefore NF2 patients and families can be assured that the best gene therapy researchers are working on curing NF2, but NF2 Biosolutions needs your support to help fund these projects.

Dr. Meyer will be the principal investigator for this NF2 project. Dr Meyer focuses on studying disease mechanisms in neurodegenerative diseases and finding new innovative therapeutic strategies for them. A main emphasis is understanding the impact of different mutations on disease course and severity. Moreover, Dr. Meyer’s lab has a strong translational focus in her projects with the goal to move additional programs towards clinical trials. These projects include the optimization of delivery strategies and evaluation of efficacy and targeting of various areas of the nervous system with gene therapy.

Dr. Kathrin Meyer

Investigators at the Center for Gene Therapy in The Research Institute at Nationwide Children’s Hospital are currently conducting numerous clinical research studies on other diseases like Batten, Charcot-Marie-Tooth Neuropathy Type 1, Duchenne Muscular Dystrophy, Mucopolysaccharidosis (MPS). See the list here.

The recently FDA approved gene therapy for treatment of the fatal genetic disorder SMA was developed at Nationwide Children’s Hospital. This approval was groundbreaking and is the first and only systemically administered gene therapy approved by the FDA in the US.

Read more about how NCH became ground zero for gene therapy by clicking on the link below:

This is also a therapy that NF2 Biosolutions are strongly endorsing, we would strongly encourage you to visit their website by clicking on the link below:

Filter News

Filter by Date
Category
Reset

Living Different: Patricks’s NF2 Blog

Read his attempt to build people's understanding of the challenges with disabilities

Read More

Beth’s Novasper Online Dog Show 2021

Find out how you can get involved in this year's fluffiest and loveable online dog show!

Read More

Christian’s Story

Christian's Mum, Ellie, share's their journey with NF & why they decided to get involved with this year's Garden Challenge!

Read More

Tate’s Shine A Light Marathon

Tate's mum shares his incredible journey with NF & why he took part in our Shine A Light Marathon to help others like him

Read More

Virtual Medical Meetings

Conferences in 2020 went online meaning the whole nursing team and key members of the head office were able to attend

Read More

Connection Coalition

NTUK joined the Connection Coalition with the aim of working together to build strong relationships & connected communities

Read More

Rare Disease Day 2021

Nerve Tumours UK joined events showcasing Rare Disease Day hosted by the Genetic Alliance on 28 February 2021

Read More

Kate, NF Mummy Community & Support

Kate tells us why she started the NF1 Mummy community group online

Read More

Alex’s story - Support in the Workplace

Alex Hetherington shares how iNForming his work colleagues about his neurofibromatosis created a supportive work environment

Read More