New Gene Therapy at a World-Renowned Research Insitute
07 August 2019
There is a new NF2 Gene Therapy Pilot Pre-Clinical Study at the Abigail Wexner Research Institute at Nationwide Children’s Hospital (NCH) by Dr. Kathrin Meyer, who is serving as the Principal Investigator.
This lab is considered to be one of the top gene therapy labs in the world, therefore NF2 patients and families can be assured that the best gene therapy researchers are working on curing NF2, but NF2 Biosolutions needs your support to help fund these projects.
Dr. Meyer will be the principal investigator for this NF2 project. Dr Meyer focuses on studying disease mechanisms in neurodegenerative diseases and finding new innovative therapeutic strategies for them. A main emphasis is understanding the impact of different mutations on disease course and severity. Moreover, Dr. Meyer’s lab has a strong translational focus in her projects with the goal to move additional programs towards clinical trials. These projects include the optimization of delivery strategies and evaluation of efficacy and targeting of various areas of the nervous system with gene therapy.
Dr. Kathrin Meyer

Investigators at the Center for Gene Therapy in The Research Institute at Nationwide Children’s Hospital are currently conducting numerous clinical research studies on other diseases like Batten, Charcot-Marie-Tooth Neuropathy Type 1, Duchenne Muscular Dystrophy, Mucopolysaccharidosis (MPS). See the list here.
The recently FDA approved gene therapy for treatment of the fatal genetic disorder SMA was developed at Nationwide Children’s Hospital. This approval was groundbreaking and is the first and only systemically administered gene therapy approved by the FDA in the US.
Read more about how NCH became ground zero for gene therapy by clicking on the link below:
This is also a therapy that NF2 Biosolutions are strongly endorsing, we would strongly encourage you to visit their website by clicking on the link below:
Filter News

NF1 & our Xander
Xander's parents have a unique fundraiser raffle, especially for LITRPG fans, with the aim of raising awareness of NF
Read More
RideLondon FreeCycle Sunday 29th May
Join Nerve Tumours UK on the official RideLondon Day 29th May 2022
Read More
RAISING THE ROOF COMEDY NIGHT
First night on the NTUK 40 years Comedy Circuit 2022 at London's Backyard Comedy Club
Read More
Chloe’s NF1 story
Chloe gives an honest assessment about coming to terms with having NF1 and how it has made her determined & strong
Read More
“Happy Easter”
A message from Karen, our Charity Director, wishing you a very Happy Easter!
Read More370x280_800_600_s_c1.jpg)
Lisa helps Shine a Light on Neurofibromatosis in Belfast
Lisa has NF1, & lobbied the Belfast Lord Mayor to get Belfast City Hall lit up blue on Neurofibromatosis Day, 17th May
Read More
Alex’s NF1 story
Alex describes her life with NF1, growing up in care, doing adaptive boxing & gym classes & getting NCFE Care qualifications
Read More
Sumeeth’s Schwannoma story
Sumeeth, thought nothing of a muscle twitch after a hangover - it was the first symptom that led to a Schwannoma diagnosis
Read More
Laura’s NF1 story
Laura is doing a skydive fundraiser to raise awareness & funds for NTUK, after her daughter was diagnosed with NF1
Read More